Stem Cells

Stem cells are the building blocks of the body. New research tries to manipulate them to help DuchenneRead more

Repurposing Drugs

Already existing drugs developed for other conditions could be helpful to those with DMDRead more

Anti-Fibrotics

Research aims to discover how to treat muscle fibre loss, where muscles are replaced by scar tissue.Read more

Utrophin Modulators

Increasing the levels of a protein called utrophin may help those with DMD regardless of their mutation typeRead more

Myostatin Inhibition

Reducing myostatin may help to make the muscles of those with DMD more healthyRead more

Gene Therapies (inc. CRISPR)

Gene therapy is the most exciting of the proposed treatments for DMD. It is working to edit the mutation that causes the diseaseRead more

Steroid Alternatives

Some promising steroid alternatives may not have the side-effects of traditional treatments.Read more

Exon Skipping And Stop Codon Read-Through

Exon skipping drugs are small pieces of genetic material that can help patch over missing parts of the gene.Read more

Treatment For The Heart

Around 90% of those with DMD have associated heart problems. New research aims to target thisRead more