Further Reading
Welcome to our library of published articles about Duchenne that we consider to be useful or of interest to those wishing to further explore aspects of the disease.
A comprehensive guide for families, published by Treat NMD, PPMD, UPPMD & MDA
A detailed paper, authored by a number of respected DMD professionals, published in the Lancet in 2010, covering Diagnosis & Management of DMD.
Challenges of Clinical Design for DMD, by Valeria Ricotti, Francesco Muntoni, Thomas Voit.
Challenges_of_clinical_trial_design_for_DMD_-_1-s2.0-S0960896615300584-main.pdf
Dr. Dongsheng Duan summarises the current status of DMD gene therapy in an interview with PPMD.
Dr_Dongsheng_Duan_2016_DMD_gene_therapy_interview.pdf
Professor Kate Bushby - Looking Forward to New Therapies: A Personal Perspective on the Translational Landscape for Muscular Dystrophies
Looking_Forward_to_New_Therapies.pdf