Dr. Manuela Corti is currently an Assistant Professor and Director of Translational Research in the Child Health Research Institute and Powell Gene Therapy Center at the University of Florida. Dr. Corti is a clinical scientist engaged in translational research focusing on understanding the contribution of neurological impairment in neuromuscular disorders by combining expertise in clinical assessment with novel therapies that rely on correcting the fundamental genetic defect. Her specific research is dedicated at developing AAV gene therapy programs for neuromuscular diseases and immunomodulation strategies to a) prevent immune responses against the AAV capsid and the transgene, and b) allow for AAV administration in pre-existing immunity. Her research interests also include outcome measures and clinical trial readiness for neuromuscular diseases such as  Friedreich’s Ataxia, Pompe disease and Duchenne Muscular Dystrophy.