Duchenne UK is a lean, ambitious and highly focused charity with a clear vision: to fund and accelerate treatments and a cure for Duchenne muscular dystrophy, to help this generation of patients with DMD.
We believe strongly in partnerships, with academics and with biotechs. We fund all research, but we focus on translational projects, using our funds to help get promising therapies out of the laboratory and into the clinic where they can help patients. We believe in funding treatments that have a chance of making it to market, providing initial funding and then staying with them on that journey.
To understand our impact and strategy please take a look at our infographic: download or open here. And read on for more detailed information about the individual projects we have funded.
Apply for funding: If you would like to discuss an idea for a research project or make a proposal for us to consider funding, please contact us in the first instance by sending an e-mail to David Bull, Director of Research: [email protected]. You can read further details here.
Duchenne UK is funding research into montelukast as a potential therapy for Duchenne Muscular DystrophyRead more
Duchenne UK is pleased to announce its support of the development of the next generation of exon skipping drugsRead more
Duchenne UK is co-funding a study into the use of elastase inhibitors to treat the symptoms of Duchenne Muscular Dystrophy (DMD) in partnership with Joining Jack and Charley's Fund.Read more
An exciting new gene-based therapy on the horizonRead more
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ReveraGen are running the clinical trial for Vamorolone which could offer a potential alternative to steroidsRead more
Our partnership with Solid Biosciences helped to advance their pre-clincial work on gene therapyRead more
A clinical trial for an anti-inflammatory drug that could reduce the thickening of the musclesRead more
Summit Therapeutics found new biomarkers for DMD that could lead to new drugs related to SMT C1100Read more
Professor Dickson explores the technique of gene editing - cutting out the mutations that cause DMDRead more
Duplications in DNA can cause DMD. We are funding gene therapy research that aims to correct this.Read more
Discovering new follow-on compounds to increase utrophin levels more effectively than SMT C1100Read more
This project looks at delivering a functioning full-size dystrophin gene via gene therapy transplicingRead more
A study to look at ways to improve stem cell transplants on a mouse model of DMDRead more
Professor Wood of Oxford University examines muscle tissue MicroRNAs to see if they are valid biomarkers for DMD.Read more
Stem cell and gene therapy combine in this new study which aims to repair muscle cells and tissueRead more
A study into the views of men with DMD about how to talk about end-of-life care and planningRead more
The project investigates how muscle fibre cells die in DMD and looks at ways to prevent thisRead more