Montelukast: Repurposing of an anti-inflammatory drug to potentially promote muscle strength and movement

Duchenne UK is funding research into montelukast as a potential therapy for Duchenne Muscular DystrophyRead more

Peptide Generation (PepGen) project

Duchenne UK is pleased to announce its support of the development of the next generation of exon skipping drugsRead more

Elastase inhibitors as a potential treatment for DMD

Duchenne UK is co-funding a study into the use of elastase inhibitors to treat the symptoms of Duchenne Muscular Dystrophy (DMD) in partnership with Joining Jack and Charley's Fund.Read more

Gene Therapy Overview

An exciting new gene-based therapy on the horizonRead more

Vamorolone (VBP15)

ReveraGen are running the clinical trial for Vamorolone which could offer a potential alternative to steroidsRead more

Solid Biosciences Gene Therapy Programme

Our partnership with Solid Biosciences helped to advance their pre-clincial work on gene therapyRead more

HT-100: A Drug To Treat Fibrosis And Inflammation

A clinical trial for an anti-inflammatory drug that could reduce the thickening of the musclesRead more

Summit Therapeutics Find New Biomarkers for DMD

Summit Therapeutics found new biomarkers for DMD that could lead to new drugs related to SMT C1100Read more

Correction Of DMD Mutations Using Genome Surgery

Professor Dickson explores the technique of gene editing - cutting out the mutations that cause DMDRead more

Genome Editing To Repair DNA Duplications

Duplications in DNA can cause DMD. We are funding gene therapy research that aims to correct this.Read more

Developing New Chemical Compounds to Target DMD

Discovering new follow-on compounds to increase utrophin levels more effectively than SMT C1100Read more

Developing Gene Therapy For DMD

This project looks at delivering a functioning full-size dystrophin gene via gene therapy transplicingRead more

Altering Muscle Environment To Change Stem Cell Behaviour

A study to look at ways to improve stem cell transplants on a mouse model of DMDRead more

Discovering Biomarkers For Duchenne Muscular Dystrophy

Professor Wood of Oxford University examines muscle tissue MicroRNAs to see if they are valid biomarkers for DMD.Read more

Repairing The Stem Cells Of People With DMD

Stem cell and gene therapy combine in this new study which aims to repair muscle cells and tissueRead more

How To Talk About End-Of-Life Care Planning

A study into the views of men with DMD about how to talk about end-of-life care and planningRead more

The Biological Process Of Muscle Fibre Death

The project investigates how muscle fibre cells die in DMD and looks at ways to prevent thisRead more