Accelerating access to treatments
We know that funding research alone is not enough to ensure that DMD patients can access the treatments they need. That's why we're going further, and breaking down barriers at every stage of drug development.
We know that funding research alone is not enough to ensure that DMD patients can access the treatments they need. That's why we're going further, and breaking down barriers at every stage of drug development.
DMD is a progressive disease, and we know that this generation of boys can't wait. That's why we've launched innovative, collaborative projects to increase the chances of treatments being tested in clinical trials, approved and made available to those that could benefit from them as soon as possible.
Selecting which DMD treatments to advance to human testing is a critical decision. In 2020, Duchenne UK joined with US-based charity Charley’s Fund to improve the data collected in preclinical research.
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Dr Emily Whitehouse is the latest consultant to join the fight against DMD at the Royal Manchester Children’s Hospital, which is part of the DMD Hub network of clinical trial sites.
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Duchenne UK has announced a further four years of funding for the DMD Hub Manager role to continue to increase DMD clinical trial capacity in the UK.
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Pfizer have announced the enrolment of their first participant in a Duchenne muscular dystrophy (DMD) gene therapy trial in the UK.
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The National Institute for Health Research has highlighted the DMD Hub as an example of how they work alongside industry to support clinical trials.
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A drug that can treat an underlying genetic cause of Duchenne muscular dystrophy has been accepted for us on NHSScotland.
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After taking part in a clinical trial, patients and their families have a right to see the data collected about them. However, they are often unable to due to several challenges around returning trial data to participants. ReveraGen BioPharma have been working to address this as part of the VISION-DMD project.
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Duchenne UK and the Project HERCULES team held a webinar to celebrate all of our achievements through this ground breaking collaboration to speed up access to treatments.
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The DMD Hub, funded by Duchenne UK, is a network of hospitals delivering clinical trials and facilitating access to treatments for the DMD community in the UK. We are pleased to share with you the DMD Hub Impact Report 2020.
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We set up HERCULES, a collaborative project to increase the chances of DMD patients accessing treatments.
Visit the HERCULES site
We founded the DMD Hub to increase the number of UK sites able to run clinical trials for DMD.
Visit the DMD Hub site
Find out about the research we fund to find the most effective treatments for DMD.
Our research
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