Accelerating access to treatments
We know that funding research alone is not enough to ensure that DMD patients can access the treatments they need. That's why we're going further, and breaking down barriers at every stage of drug development.
We know that funding research alone is not enough to ensure that DMD patients can access the treatments they need. That's why we're going further, and breaking down barriers at every stage of drug development.
DMD is a progressive disease, and we know that this generation of boys can't wait. That's why we've launched innovative, collaborative projects to increase the chances of treatments being tested in clinical trials, approved and made available to those that could benefit from them as soon as possible.
Duchenne UK and the DMD Hub are launching a new pilot project aiming to provide fair and equal access to DMD trials across the UK
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In a new transatlantic collaboration, Duchenne UK and the DMD Hub, PPMD and RTI International are conducting a study to explore attitudes towards gene therapy and gene editing from adults with Duchenne muscular dystrophy (DMD), parents and caregivers of children with DMD, and clinicians.
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The Clinical Trials Lectureship grant enabled Dr Michela Guglieri to act as the Clinical Research Team Leader within the John Walton Muscular Dystrophy Research Centre in Newcastle
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In the last few months, the DMD Hub has recruited two new staff members to work with Emma Heslop, the DMD Hub Manager, and to look at new areas where the DMD Hub can develop support.
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The European Medicines Agency (EMA) has approved the first measure collected using a digital wearable device for use in clinical trials for Duchenne muscular dystrophy.
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Duchenne UK and Project HERCULES announce the launch of a new patient centred, quality of life tool designed to support faster access to new treatments for people living with Duchenne muscular dystrophy
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We're funding more posts as part of the DMD Hub so that more boys are now able to take part in trials for potentially life-changing treatments.
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Selecting which DMD treatments to advance to human testing is a critical decision. In 2020, Duchenne UK joined with US-based charity Charley’s Fund to improve the data collected in preclinical research.
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Dr Emily Whitehouse is the latest consultant to join the fight against DMD at the Royal Manchester Children’s Hospital, which is part of the DMD Hub network of clinical trial sites.
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We set up HERCULES, a collaborative project to increase the chances of DMD patients accessing treatments.
Visit the HERCULES site
We founded the DMD Hub to increase the number of UK sites able to run clinical trials for DMD.
Visit the DMD Hub site
Find out about the research we fund to find the most effective treatments for DMD.
Our research
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