What is a Clinical Trial?

Clinical trials are research studies that explore whether a medical treatment, drug, procedure or device is safe and effective for humans. 

Clinical trials are an important part of the evidence-based process for making new treatments available to patients. They produce the best possible data for healthcare decision-makers.  

They are required by the Medicines and Healthcare Products Regulatory Agency (MHRA) which licence new medicinal products in the UK. Doctors can only use drugs, procedures and devices with this licence to treat their patients. 

The DMD Hub has lots of information to help you understand about clinical trials and things you may need to consider. Click the links below to find out about: 

You can find all the clinical trials for DMD in the UK in our Clinical Trial Finder.

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Duchenne UK are here to offer support and advice. If you have any questions, please get in touch on [email protected]