Duchenne UK supporters invited to celebrate Captain Sir Tom's achievements in special fundraising event

Duchenne UK is proud to be inviting our supporters to take part in Captain Tom 100, a new fundraising initiative which invites people around the world to take on a challenge based around the number 100. Read more

PepGen present latest data from new exon skipping therapy for Duchenne muscular dystrophy

Biotech company PepGen presented the latest data from their research into a new exon-skipping treatment for Duchenne muscular dystrophy at the 2021 Muscular Dystrophy Association Clinical and Scientific Conference last week. Read more

Returning individual clinical trial data back to patients – VISION-DMD project update

After taking part in a clinical trial, patients and their families have a right to see the data collected about them. However, they are often unable to due to several challenges around returning trial data to participants. ReveraGen BioPharma have been working to address this as part of the VISION-DMD project. Read more

Duchenne UK is hiring!

Duchenne UK is seeking a Director of Research and Clinical Development, who has hands-on experience of drug discovery and development. We are seeking a well networked candidate who can identify and critically assess new drug targets that exhibit the potential to transform the treatment of Duchenne muscular dystrophy. Read more

Four charities call on Scottish Medicines Consortium to approve treatment for Duchenne muscular dystrophy

Together with Muscular Dystrophy UK, Action Duchenne and Duchenne Family Support Group, Duchenne UK are asking the SMC to approve a drug called Translarna. It is the first drug that can help treat cases of an underlying cause of Duchenne muscular dystrophy. Read more

Courier Post Logistics Ltd announces £1m support to Duchenne UK.

Duchenne UK is delighted to announce a new partnership with Cheshire-based business Courier Post Logistics. They have committed to raising an incredible £1m towards our work. Read more

Recommendations to bring gene therapy trials for Duchenne Muscular Dystrophy to the UK are published

Important findings about the readiness of the UK to host clinical trials in gene therapy have been published in the Journal for Neuromuscular Disorders. Read more

Duchenne UK welcomes new members to its Scientific Advisory Board

Given the expanding remit of Duchenne UK’s work and the variety of projects which we support, we are delighted to announce that four new researchers will be joining our Scientific Advisory Board. Read more

Statement by neuromuscular clinicians: COVID vaccines are safe

A statement from four neuromuscular clinicians confirms that COVID-19 vaccines can be taken by people with DMD, and encourage those who are eligible to take it. Read more

National Strategy for Disabled People survey

The Government's Disability Unit is conducting a survey for disabled people and carers to help inform the National Strategy for Disabled People planned for Spring 2021. Read more

Translarna - January 2021 update

NICE have scheduled a re-review of Translarna to be completed in July 2021. Click to read more. Read more