This will be a pilot study in non-ambulatory patients to test it's benefits. Read more
We are pleased to share with you our Impact Report 2019. Thank you for helping us grow from a tiny patient organisation to a multi-million pound catalyser and funder of research. Read more
The DMD Hub team brought together 100 stakeholders to understand what more can be done to be bring gene therapy trials to the UK. Read more
Last week, Dr David Bull, our Director of Research, attended the conference in Leiden. It's an important meeting for patient advocacy, DMD research and to meet with our many research partners. Read more
Money raised will fund clinical trials, doctors’ posts and new research into finding a cure for DMD Read more
We are very pleased to be able to share with you our first ever DMD Hub Impact Report. The DMD Hub is a network of hospitals expanding clinical trial capacity in the UK for Duchenne muscular dystrophy. Read more
The Nutraceutical project with Reading University has unfortunately been terminated due to practical and technical issues. Read more
William Eames will walk out onto the pitch at Allianz Park alongside his grandfather Peter Godfrey to deliver the match ball ahead of kick-off at Saracens Champions Cup match on Saturday. Read more
At our gene therapy meeting Emily and Alex gave a speech about the importance of the patient perspective. 100+ representatives from NICE, the NHS, UK hospitals and pharma attended Read more
Our meeting, organised through the DMD Hub, brings together 100 partners from hospitals around the UK and the pharmaceutical industry to discuss bringing gene therapy trials to the UK. Read more
In October 2019, results from a trial testing the combination treatment of Metformin and L-Citruline were published. Read our summary paper on the results. Read more
This week, our CEO Emily Crossley will be travelling to Copenhagen to present on Project HERCULES at the ISPOR conference, the go-to place for those who work in Health Technology Assessment (HTA). Read more