Number of children on clinical trials doubles at Great Ormond Street Hospital, following funding through the DMD Hub

Duchenne UK is pleased to share a report from Great Ormond Street about the positive impact of the clinical staff posts we fund at the hospital.Read more

Welcome to DUCHENNEBER

A whole month dedicated to raising awareness and funds for research into Duchenne Muscular Dystrophy. Each day on our DUCHENNEBER ADVENT CALENDAR we will feature news about research projects, new resources for the community, videos & podcasts.Read more

BREXIT: the impact on medical innovation and patients with Duchenne Muscular Dystrophy in the UK

This document highlights some of the major challenges Brexit poses to research and access to medicines for patients with DMDRead more

Duchenne UK’s Project HERCULES Awarded Prestigious Rare Disease Award

Duchenne UK’s Project HERCULES has been awarded the 2019 EURORDIS Black Pearl Award for Patient Engagement for outstanding commitment in the rare disease community.Read more

Duchenne UK grants £655,000 to Evox Therapeutics to investigate new ways of delivering gene therapy to patients

We will look at whether it is possible to deliver the dystrophin gene using exosomes rather than a virus.Read more

Jon Rey-Hastie reflects on Duchenne UK's Rugby Dinner

Jon Rey-Hastie, CEO of DMD Pathfinders reflects on our rugby fundraising dinner for the World's Strongest Boy: An evening with Jonny Wilkinson and Owen Farrell, which raised £400,000. Thank you to everyone who came and supported us.Read more

Duchenne UK attends the World Muscle Society 2018 Conference

David Bull, Duchenne UK’s Director of Research, attended the World Muscle Society (WMS) Congress 2018 on neuromuscular disorders in Mendoza, Argentina earlier this month.Read more

Focus On Caring For The Heart In Duchenne Muscular Dystrophy

This month a Cochrane review was published in which the focus was on drugs currently used to prevent or treat heart complications in DMD, Becker MD, and X-linked dilated cardiomyopathyRead more

Update on Simvastatin as a potential treatment for DMD

Duchenne UK funds €35,745 to further research Simvastatin as a potential treatment for DMD. Dr Annemieke Aartsma-Rus at Leiden University Medical Centre will perform a replication study to validate Dr Froehner’s work.Read more

Outcome measures for DMD clinical trials

We work with scientists and researchers to look at how to improve the outcomes of clinical trials and ensure companies are using the right measurements to determine whether or not a drug in a clinical trial is working or not.Read more

Duchenne UK attend meeting for All-Party Parliamentary Group On Off-Patent Drugs

Yesterday, representatives from Duchenne UK attended an All-Party Parliamentary Group (APPG) on off-patent drugs in parliament chaired by Nick Thomas-Symonds MP.Read more