Access to treatments, Policy and campaigning
Wes Streeting MP, offers help for our EAP campaign
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Access to treatments, Policy and campaigning
Breaking News: First clinic doses patients with givinostat under Early Access Programme
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Access to treatments, Policy and campaigning
On Rare Disease Day 2025, a message from our founders, Emily and Alex
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Access to treatments, Policy and campaigning
The givinostat EAP – a promising new medication with hurdles to implementation
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Access to treatments, Policy and campaigning
Speaking truth to power: an extraordinary update on our #Time is Muscle campaign
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