Access to treatments, DMD research, Policy and campaigning
Update on Sarepta and Roche’s SRP-9001 gene therapy
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Access to treatments, DMD research, Policy and campaigning
Sarepta and Roche’s SRP-9001 – FDA Advisory Committee meeting
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Patient care & support
Parent Information Day 2023
We were delighted to welcome dozens of families to our latest Parents Information Day in London this weekend. We are so grateful for all those who came. People came from across the country – one Duchenne researcher came from Boston in the United States! There were presentations from a range of specialists – and the […]
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Access to treatments, Policy and campaigning
Duchenne UK statement on VPAS
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