Latest news - Duchenne UK
Interim decision: ataluren (Translarna) not recommended for NHS
NICE has released draft guidance which does not recommend the use of ataluren on the NHS for the treatment of Duchenne muscular dystrophy (DMD) with a nonsense mutation in the dystrophin gene.
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Study paves the way for improved detection of heart disease in female carriers of DMD
A recent report from a study funded by Duchenne UK has improved understanding of early detection of heart muscle disease in female carriers of Duchenne muscular dystrophy (DMD), paving the way for further research.
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Women and Duchenne – Jo Eames, DMD mum and fundraiser
Jo tells her story of her son's diagnosis and daily life with DMD as a mother and caregiver for World Duchenne Awareness Day 2022
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Women and Duchenne – Fleur Chandler, Project HERCULES Chair
Fleur Chandler is a health economist and currently Head of Market Access at Sanofi, a worldwide pharmaceutical and healthcare company. She is also mum to Dominic, a 16-year-old boy living with DMD.
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Women and Duchenne – Dr Alessandra Gaeta, Director of Research
Alessandra speaks about her career in science and what's going on the DMD research world for World Duchenne Awareness Day 2022
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Join the Duchenne UK team
Duchenne UK has two exciting new opportunities for a Communications Officer and Programme Manager to work with us. Could you join our small, friendly and passionate team in London and be part of our mission to end Duchenne?
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More clinical trials for DMD running in Glasgow thanks to the DMD Hub
By funding staff posts at the Royal Hospital for Children, Glasgow, the DMD Hub has enabled more trials to take place and more boys in Scotland to take part in research
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Psychological and psychiatric support put in place for DMD patients and families
Dedicated specialist support for Duchenne muscular dystrophy (DMD) patients and families’ mental health and wellbeing will soon be more readily available, as part of the DMD Care UK project.
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NICE release statement on continued access to ataluren (Translarna)
NICE and NHS England have released a statement about continued access for DMD patients currently being treated with ataluren
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