Duchenne UK is a lean, ambitious and highly focused charity with a clear vision: to fund and accelerate treatments and a cure for Duchenne Muscular Dystrophy (DMD), and to do so in a decade.

DMD is a devastating muscle wasting disease and is the most common genetic killer of children worldwide. We aim to eradicate it in 10 years: TO END DUCHENNE IN TEN.

We are the UK’s leanest Duchenne research charity. In the last 6 years (as Duchenne Children's Trust and Joining Jack) Duchenne UK has raised over £15 million

We've spent £8m to date and committed a further £6m to accelerating research.

We have achieved some incredible results, with the help of donors, partner charities and researchers, for details please read:  Our Impact.

We have an innovative approach to funding. Not only do we fund basic research, but we fund clinical trials. We fund the doctors and nurses in the UK to deliver those trials: and we look at where ever possible, we can accelerate research and work with industry and regulators to get drugs approved.

To achieve our mission, we adopt an integrated approach that has 3 main areas of activity/focus.

1) Funding Research and Trials:

Our approach is sharply focused on advancing research – and getting treatments into the clinic and to patients as quickly as possible. We actively seek out projects and possible therapies that could benefit this generation of patients. We invest globally in both basic science and translational research.

Read more here about the research projects and clinical trials that we fund. 

2) Accelerating Drug Development:

Funding the research is the first crucial step. But funding research on its own it isn’t enough. So we proactively invest in every stage of the drug development timeline to improve and accelerate the process.

Read more here about how we accelerate drug development through our own initiatives and by working both globally and in the UK with industry, governments and health providers. 

3) Community Engagement & Support:

Patients with DMD are at the heart of everything we do. Duchenne UK was set up by parents to fight every day to speed up treatments for all those living with DMD. Our drive and ambition comes from our deep understanding of the pain and the challenges that families face. 

Read here about how we engage with the Duchenne community and collaborate with other charities to improve the life of those living with Duchenne.

Duchenne UK is a member of the AMRC.