Real results that make a real difference
OUR IMPACT
Our impact is measured by the tangible improvements we deliver in care, treatment access, and research. Since our founding, Duchenne UK has invested millions into research and infrastructure. Here’s what that means for families living with Duchenne muscular dystrophy.
What we’ve achieved
Increased clinical trials and participation
Helped kickstart the gene therapy revolution in Duchenne
Funded the first ever treatment to treat all patients with Duchenne regardless of their genetic mutation
Access to two new treatments for Duchenne
Set new standards of care
Brought the patient voice to industry, regulators and decision-makers
Our investment
in research
34
Posts in the Duchenne
Clinical Trial Network
106
Projects funded
£15M
£15M of which £3.3M towards research infrastructure and the rest largely towards therapeutic development
The impact of our funding
11
Duchenne Hub UK clinical trial sites
574
Enabled 574 people with Duchenne take part in a clinical trial
41
Duchenne Hub UK has run 41 clinical trials
81
Supported 81 clinical trials, accelerating the development of new treatments for Duchenne
10
10 best practice care guidelines promoting best care for all
Impact reports
You can read more about these achievements in our impact reports
