Regulatory approval for ELEVIDYS in the UK on hold
NICE recognises DMD Care UK’s clinical guidelines for cardiac care
Statement from NorthStar Network of UK clinicians regarding givinostat
Duchenne UK accelerates development of gene editing therapy
Exon skipping trial did not meet primary end point
NICE reviews respiratory care guideline
NICE requests second committee meeting
Scottish Medicines Consortium (SMC) approves a new treatment for use on the NHS in Scotland
Alex shares his family’s journey of resilience and hope
